Clinical trials for Spinal muscular atrophy

Information provided by WHO International Clinical Trials Registry

The clinical trials below are relevant to Spinal muscular atrophy. For all clinical trials, go to clinical trials search

This list shows clinical trials for Spinal muscular atrophy

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  • Spinal muscular atrophy
Title Recruitment status Location
A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies. Recruiting United Kingdom
A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of RO7034067 in Type 2 and 3 Spinal Muscular Atrophy Participants (Sunfish) Recruiting United Kingdom
A Phase 3, Randomized, Double-blind, Sham-Procedure Controlled Study to Assess the Clinical Efficacy and Safety of ISIS 396443 Administered Intrathecally in Patients With Infantile-onset Spinal Muscular Atrophy Recruiting United Kingdom
A Study to Evaluate Long Term Safety, Tolerability, and Effectiveness of Olesoxime in Patients With Spinal Muscular Atrophy Recruiting United Kingdom
An extension study for patients with Spinal Muscular Atrophy who participated to the previous ISIS 396443 studies Not Recruiting United Kingdom
A controlled clinical study to assess the effectiveness and safety of ISIS 396443 in patients with infantile-onset Spinal Muscular Atrophy Not Recruiting United Kingdom
Phase II, multicenter, randomized, adaptive, double-blind, placebo controlled study to assess safety and efficacy of olesoxime (TRO19622) in 3-25 year old Spinal Muscular Atrophy (SMA) patients. Not Recruiting United Kingdom
Phase II, multicenter, randomized, adaptive, double-blind, placebo controlled study to assess safety and efficacy of olesoxime (TRO19622) in 3-25 year old Spinal Muscular Atrophy (SMA) patients. Not Recruiting United Kingdom
A controlled clinical study to assess the effectiveness and safety of ISIS 396443 in patients with infantile-onset Spinal Muscular Atrophy Not Recruiting United Kingdom
Phase II, multicenter, randomized, adaptive, double-blind, placebo controlled study to assess safety and efficacy of olesoxime (TRO19622) in 3-25 year old Spinal Muscular Atrophy (SMA) patients. Not Recruiting United Kingdom

Page last reviewed: 09/03/2015

Next review due: 01/04/2017